One year follow-up of Risdiplam monotherapy in children with spinal muscular atrophy: A case series report
LIU Fangfang, WANG Jie, GUO Xiaohua, ZHANG Huawei, WANG Dong, LIU Qingfeng, ZHEN Yuanyuan, SONG Jiguo, MA Kai
Chinese Journal of Evidence-Based Pediatrics . 2024, (2): 93 -97 .  DOI: 10.3969/j.issn.1673-5501.2024.02.003