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Welcome to Chinese Journal of Evidence-Based Pediatrics,Today is
ISSN 1673-5501 CN 31-1969/R
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One year follow-up of Risdiplam monotherapy in children with spinal muscular atrophy: A case series report
LIU Fangfang, WANG Jie, GUO Xiaohua, ZHANG Huawei, WANG Dong, LIU Qingfeng, ZHEN Yuanyuan, SONG Jiguo, MA Kai
Chinese Journal of Evidence-Based Pediatrics . 2024, (
2
): 93 -97 . DOI: 10.3969/j.issn.1673-5501.2024.02.003